News

Roche (SIX:ROG) shares dropped 2% on Monday after the company paused dosing of its gene therapy Elevidys in non-ambulatory ...
Sarepta Therapeutics shares plunged 36% after the company reported a second case of acute liver failure resulting in death from taking Elevidys, which is a gene therapy for patients with Duchenne ...
Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today provided a safety ...
The drug, Givinostat, has been approved as safe for use but Belfast Health Trust, NI's specialist centre for the condition, ...
Participants with Duchenne muscular dystrophy (DMD) who received RGX-202 demonstrated functional improvement and better ...
Parents of children with an incurable muscle-wasting condition have called on the Minister for Health to accelerate the ...
U.S. FDA successfully completed Pre-License Inspection; Company expects facility will meet all requirements to support ...
The parents of a nine-year-old boy battling a devastating muscle-wasting condition say new research could offer them more ...
The campaign to commemorate the work of the Muscular Dystrophy Association was created in partnership with agency Yes&.